our experience.
Our experience spans a number of areas including genetic and rare diseases.
disease states
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novel mechanisms
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rare & genetic diseases
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neurology
acute ischemic stroke, amyotrophic lateral sclerosis, alzheimer’s, angelman’s syndrome, cerebral adrenoleukodystrophy, epilepsy, essential tremor, fragile x syndrome, migraine, multiple sclerosis, spinal muscular atrophy, super refractory status epilepticus
oncology
acute myeloid leukemia, cancer-associated thrombosis, glioblastoma, hepatic veno-occlusive disease, multiple myeloma, prostate cancer
pulmonology
COPD, cystic fibrosis, idiopathic pulmonary fibrosis, interstitial lung disease
ophthalmology
diabetic macular edema, dry eye disease, glaucoma, inherited retinal dystrophy
hematology
β-thalassemia, hemophilia, paroxysmal nocturnal hemoglobinuria, sickle cell disease
immunology
osteoarthritis, psoriasis, seasonal allergic rhinitis, systemic sclerosis, ulcerative colitis
mental health
major depressive disorder, postpartum depression, schizophrenia
other
hereditary tyrosinemia type 1, IBS, IBD, overactive bladder, pain, visceral pain